International Conference On Orphan Drugs and Rare Diseases

August 17-19, 2023

August 17 -19, 2023 | Online Event

Translational Science

Translational Science

Translational research aims to provide more relevant, usable outcomes that enhance human health directly. The purpose of translational research is to more rapidly and efficiently convert (move) basic science discoveries into practise. Translational science is a branch of research dedicated to deciphering the scientific and operational concepts that underpin each step of the translational process. Rare diseases are a driving force behind medical and pharmacological innovation and improvement. The majority of rare diseases are genetic disorders or atypical manifestations of infectious, immunologic, or oncologic diseases; they all allow researchers to explore the extremes of human pathology and gain insight into normal and abnormal physiology. Drug development has recently shifted its attention to predominantly genetic classification of diseases, allowing for the identification of molecularly defined targets and the creation of targeted therapeutics. Translational research has the potential to transfer promising research into practical new medicines for people suffering from rare diseases.

  • Diagnosis
  • Clinical Trial Design
  • Need for Translational Research
Orphan Drugs 2023 Speakers
Speaker at Orphan Drugs and Rare Diseases 2023 - Vicki Ratner

Vicki Ratner

ESSIC - International Society for the Study of BPS, United States
Speaker at Orphan Drugs and Rare Diseases 2023 - Kondakova O. B

Kondakova O. B

National Medical Research Center for Children's Health Federal state autonomous institution of the Russian Federation Ministry of Health, Russian Federation
Speaker at Orphan Drugs and Rare Diseases 2023 - Paul L Kaufman

Paul L Kaufman

University of Wisconsin-Madison, United States
Speaker at Orphan Drugs and Rare Diseases 2023 - Magali Taiel

Magali Taiel

GenSight Biologics, France

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