University of Miami, United States

Title: Ectopically expressed olfactory receptors as an untapped family of drug targets. Discovery of agonists and antagonists of OR51E1, an understudied G protein-coupled receptor

Jeeva Clinical Trials, Inc, United States

Title: Emerging solutions for inclusive orphan drug clinical trials management

The Russian University of Medicine & Russian Academy of Natural Sciences, Russian Federation

Title: Personalized and Precision Medicine (PPM) as a unique healthcare model to secure the human healthcare and biosafety among childhood

La Jolla Labs, United States

Title: Democratizing ASO drug discovery at La Jolla Labs

The Progeria Research Foundation, United States

Title: About progeria - The ultra-rare, fatal "rapid-aging" disease - And how you can help

National Center for rare Diseases - Istituto Superiore di Sanita, Italy

Title: The person, not the disease: emotional and social aspects of rare diseases

ITMO University, Russian Federation

Title: Novel polyphenolic compounds from Mangifera indica as promising alternatives for treating strongyloides stercoralis infections

Torbat Heydariyeh University of Medical Sciences, Iran (Islamic Republic of)

Title: Recent advances in orphan drug development: From research to clinical application

2nd International Conference on Orphan Drugs and Rare Diseases

Orphan Drugs 2025