HYBRID EVENT: You can participate in person at Rome, Italy or Virtually from your home or work.

2nd International Conference on Orphan Drugs and Rare Diseases

March 17-19, 2025

March 17 -19, 2025 | Rome, Italy

Orphan Drugs 2023

Speaker at Orphan Drugs and Rare Diseases 2023 - Kondakova O. B
National Medical Research Center for Children's Health Federal state autonomous institution of the Russian Federation Ministry of Health, Russian Federation

Title: Rare forms of primary enzyme defects in monoamine biosynthesis: AADCD and TH-deficient progressive infantile encephalopathy

Speaker at Orphan Drugs and Rare Diseases 2023 - Kranthi Kumar Singamaneni
Chaitanya Bharathi Institute of Technology, India

Title: Cyber security role for rare diseases and pharmaceutical industry

Speaker at Orphan Drugs and Rare Diseases 2023 - Zeynep Unluturk
University of Health Sciences Kocaeli Derince Training Hospital, Turkey

Title: Neiman-Pick disease Type C- early onset dementia

Speaker at Orphan Drugs and Rare Diseases 2023 - Vicki Ratner
ESSIC - International Society for the Study of BPS, United States

Title: Interstitial cystitis/bladder pain syndrome - A rare disease?

Speaker at Orphan Drugs and Rare Diseases 2023 - Paul L Kaufman
University of Wisconsin-Madison, United States

Title: Gene and stem cell therapy for glaucoma

Watsapp