International Conference On Orphan Drugs and Rare Diseases
August 21-23, 2023
Orphan Drugs 2023
Title: Data integration for drug repurposing in rare diseases, A case study of glioblastoma
Title: What does a technology-enabled patient concierge mean to the orphan drugs industry?
Title: Repurposing clofazimine for efficacy in mesothelioma – in-vitro and ex-vivo evaluation
Title: Review of diagnosis and therapeutics for management of familial chylomicronemia syndrome
Title: Multi-tasking by the Mowat-Wilson Syndrome transcription factor ZEB2
Title: Progress related in genetic research on Kawasaki disease
Title: The foundation for rare disease and its role in the european rare disease research landscape
Title: Lumevoq gene therapy in leber hereditary optic neuropathy
Title: Autoimmunity to the autonomic nervous system-The clue for many clinical entities
Title: Interstitial Cystitis/Bladder Pain Syndrome - a rare disease?
