HYBRID EVENT: You can participate in person at London, UK or Virtually from your home or work.

International Conference On Orphan Drugs and Rare Diseases

August 21-23, 2023

August 21 -23, 2023 | London, UK

Pharmacology and Toxicology

Pharmacology and Toxicology

Due to the unique characteristics of rare diseases, developing medications for them might be difficult. The rarity of a condition makes drug development difficult. Due to a paucity of people, well-designed clinical trials to demonstrate efficacy can be difficult to conduct, and studies substantial enough to determine major hazards are nearly impossible to do. When no other options are available, patients may be ready to risk side effects in exchange for potential benefits, but the benefit-to-harm balance is difficult to quantify and may be unfavourable in some situations. Clinical pharmacology, a translational discipline, is a critical component of drug development, including therapeutic development for rare diseases. Health administrators have financial challenges when it comes to innovative pharmaceuticals, particularly orphan drugs. Individual rare disorders impact a small number of people, yet they collectively affect a significant portion of the population. They require our assistance.

  • Drug Repurposing
  • Safety Assessment
  • Clinical Trials
  • Patient Involvement
  • Translational Research
  • Clinical Pharmacology
  • Orphan Drug Development
Committee Members
Speaker at Orphan Drugs and Rare Diseases 2023 -  Daniel Scherman

Daniel Scherman

Fondation Maladies Rares, France
Speaker at Orphan Drugs and Rare Diseases 2023 -  Jiao Fuyong

Jiao Fuyong

Children’s Hospital of Shaanxi Provincial People’s Hospital, China
Speaker at Orphan Drugs and Rare Diseases 2023 -  Victor Shengkan jin

Victor Shengkan jin

Rutgers University, United States
Orphan Drugs 2023 Speakers
Speaker at Orphan Drugs and Rare Diseases 2023 - Candida Fratazzi

Candida Fratazzi

BBCR Consulting - Massachusetts, United States
Speaker at Orphan Drugs and Rare Diseases 2023 - Philip Bielefeld

Philip Bielefeld

Avignon Hospital, France
Speaker at Orphan Drugs and Rare Diseases 2023 - Harsha Rajasimha

Harsha Rajasimha

Jeeva Informatics Solutions Inc, United States

Submit your abstract Today

Watsapp