International Conference On Orphan Drugs and Rare Diseases

August 17-19, 2023

August 17 -19, 2023 | Online Event

Access and Pricing

Access and Pricing

Pharmaceutical companies have been increasingly focusing on developing treatments for rare diseases in recent years. This is largely due to technological advancements that make identifying the genetic causes of rare diseases easier. Because of their high prices, orphan medications have a lot of potential to generate income. By 2022, the global orphan medication industry is expected to have grown to $209 billion, accounting for 21.4 percent of all branded prescription drug sales. The high pricing connected with some orphan drugs have become a point of contention as the number of approved orphan drugs has grown. The high expense of drug development and recouping these costs by a smaller patient pool are the most common reasons for orphan medicine prices. We can't use cost-based pricing strategies unless we fully grasp the costs of orphan medicine research. If the patient population is limited enough, orphan medications with relatively low research costs may nonetheless require very high pricing to recoup those expenditures. Even if a more accurate cost of medication development at the drug level becomes accessible, the question of how much profit should be allowed above the cost of drug development remains. There is still a lot of work to be done in this area to better understand how to reward innovation while keeping drug expenditures in check.

  • Cost Based Pricing
  • Establishing A Reasonable Price
  • Reimbursed Price
  • Patient Access
Orphan Drugs 2023 Speakers
Speaker at Orphan Drugs and Rare Diseases 2023 - Vicki Ratner

Vicki Ratner

ESSIC - International Society for the Study of BPS, United States
Speaker at Orphan Drugs and Rare Diseases 2023 - Kondakova O. B

Kondakova O. B

National Medical Research Center for Children's Health Federal state autonomous institution of the Russian Federation Ministry of Health, Russian Federation
Speaker at Orphan Drugs and Rare Diseases 2023 - Paul L Kaufman

Paul L Kaufman

University of Wisconsin-Madison, United States
Speaker at Orphan Drugs and Rare Diseases 2023 - Magali Taiel

Magali Taiel

GenSight Biologics, France

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